Eme has been robbed of her sight by LCA-CRB1, a very rare genetic disease. By age 3, she was already blind.
LCA-CRB1 has no treatment. A gene therapy clinical trial is being conducted for LCA-RPE65 right now that is working and is giving blind kids like Eme their sight back! By replacing the mutated/broken gene with a good copy of the gene, blind kids can see again! Join us & help raise awareness of childhood blindness from LCA (Lebers Congenital Amaurosis).
Are you the parent, friend, loved one or caregiver of someone struggling with LCA? Join in the conversation.
Questions? Feel free to contact us.